Infant With Incurable Disease is First to Successfully Receive Personalized Gene Therapy Treatment
KJ with his parents and siblings after first-of-its-kind personalized gene editing therapy –Credit: Children’s Hospital of Philadelphia In a historic medical breakthrough, a child diagnosed with a rare genetic disorder has been successfully treated with a customized CRISPR gene editing therapy by a team at Children’s Hospital of Philadelphia and Penn Medicine. The infant, KJ, … Read more