Researchers at University of California San Diego School of Medicine have developed a gene therapy for Alzheimer’s disease that could help protect the brain from damage and preserve cognitive function. Unlike existing treatments for Alzheimer’s that target unhealthy protein deposits in the brain, the new approach could help address the root cause of Alzheimer’s disease … Read more
Until recently, even the most advanced gene therapies could only be given after a child was … More born—often racing against time to prevent irreversible damage. Image by freepik In the first part of this series, we explored how early genetic screening and gene therapy transform the lives of newborns and their families. Now, we’re … Read more
Archyde: Latest World News, Economy, Entertainment, Health, Technology & Sports Updates “`html Personalized Gene Therapy: A New Era for Rare Diseases Personalized Gene Therapy: A New Era for Rare Diseases Imagine a future where genetic diseases,once considered incurable,can be precisely targeted and treated with therapies tailored to an individual’s unique genetic makeup. This future is … Read more
Novartis Seeks Marketing Assistant for Haematology Team in London CITY – May 3, 2024 – Global healthcare leader Novartis is hiring a Marketing Assistant for their haematology team in London, as announced today. Teh role, based in London, aims to support the company’s efforts in delivering value to customers and patients. The primary responsibilities will … Read more
“`html { “@context”: “https://schema.org”, “@type”: “NewsArticle”, “headline”: “Genespire Advances Gene Therapy for MMA: Preclinical Data unveiled”, “description”: “Genespire announced positive preclinical results for its gene therapy, marking a important step forward.”, “datePublished”: Genespire Advances Gene Therapy for MMA: Preclinical data Unveiled Gene Therapy Breakthrough for Methylmalonic Acidemia Milan, Italy – Genespire, a biotechnology firm specializing … Read more
PRESS RELEASE Preclinical insights into dosing for first-in-human in vivo liver-directed gene therapy for MMA delivered in an oral presentation at the ASGCT Annual Meeting Milan, ITALY – 14 May 2025 – Genespire, a biotechnology company developing off-the-shelf gene therapies for pediatric patients affected by genetic diseases, presented positive preclinical insights into dosing for the … Read more
Over the past few years interest has ramped up across industry and academia in bringing advanced cell therapy modalities such as chimeric antigen receptor T-cell (CAR-T) therapy to the field of autoimmune disease, with many directing their initial efforts at systemic lupus erythematosus (SLE) and lupus nephritis (LN). Thus far, late 2024 and early 2025 … Read more
According to the Michael J. Fox Foundation, almost 1 million people in United States live with Parkinson disease (PD) and more than 6 million people in the world live with PD. Notably, the symptoms of PD and their severity vary widely, and can be different for every person. Although some treatment options for the disease … Read more
This article originally appeared on our sister site, Ophthalmology Times Europe®. Nanoscope Therapeutics’ MCO-010 (sonpiretigene isteparvovec), an investigational ambient-light activatable multi-characteristic opsin (MCO) gene therapy, showed the ability to restore vision in patients with retinitis pigmentosa (RP) in clinical data published Molecular Therapy.1 In the paper, which is entitled “A synthetic opsin restores vision in patients … Read more
This is the second part of an interview with David-Alexandre Gros, MD. For the first part, click here. David-Alexandre C. Gros, MDCredit: Eledon EGenesis’s EGEN-2784 is a porcine kidney that features a number of genetic modifications intended to prevent rejection in human patients, and is under evaluation for the treatment of end-stage kidney disease alongside the … Read more