Personalized gene editing corrects fatal infant metabolic disorder in world-first treatment

In a global first, scientists have used advanced base editing to repair a deadly gene mutation in a newborn, marking a major leap forward in the treatment of rare inherited metabolic diseases. Study: Personalized Gene Editing to Treat an Inborn Error of Metabolism. Image Credit: Shutterstock AI Generator / Shutterstock.com In a recent New England Journal … Read more

Newly discovered Cat1 protein halts viral infections by depleting cellular fuel

Every living creature on Earth needs to protect itself from things that would do it harm. Bacteria are no different. And despite their relative simplicity, they deploy remarkably savvy defensive strategies against viral invaders. The most well-known is CRISPR-Cas9, adapted for human use as the first FDA-approved genetic editing technique. In the past year, researchers … Read more

Gene-edited immune cells show promise against advanced GI cancers

Researchers at the University of Minnesota have completed a first-in-human clinical trial testing a CRISPR/Cas9 gene-editing technique to help the immune system fight advanced gastrointestinal (GI) cancers. The results, recently published in Lancet Oncology, show encouraging signs of safety and potential effectiveness of the treatment. “Despite many advances in understanding the genomic drivers and other … Read more

Bacteria use dormant phages to create immunity against viral invaders

Like people, bacteria get invaded by viruses. In bacteria, the viral invaders are called bacteriophages, derived from the Greek word for bacteria-eaters, or in shortened form, “phages.” Scientists have sought to learn how the single-cell organisms survive phage infection in a bid to further understand human immunity and develop ways to combat diseases. Now, Johns … Read more

Groundbreaking study unveils key mechanism for neuronal identity regulation

A team of researchers from the Institute for Neurosciences, a joint center of the Spanish National Research Council (CSIC) and the Miguel Hernández University (UMH) of Elche, in collaboration with researchers from Columbia University (New York, USA), has identified a mechanism that regulates the production of two different proteins from the same gene. This discovery, … Read more

Revolutionizing Regenerative Medicine: The Advancements and Potential of CRISPR Technologies in Tissue Repair and Disease Treatment

Harnessing the Power of CRISPR in Regenerative Medicine: A Comprehensive Look In recent years, CRISPR/Cas9 technologies have emerged as groundbreaking tools in the rapidly evolving field of regenerative… The post Revolutionizing Regenerative Medicine: The Advancements and Potential of CRISPR Technologies in Tissue Repair and Disease Treatment appeared first on NewsyList. Source link